Homology Medicines IncChange company Symbol lookupSelect an option...FIXX Homology Medicines IncFTDR Frontdoor IncHD Home Depot IncSRCE 1st Source CorpPNC PNC Financial Services Group IncAAPL Apple IncMSFT Microsoft CorpFAZE FaZe Holdings IncSSP E W Scripps CoNHWK NightHawk Biosciences IncGo
Homology Medicines, Inc. is a clinical-stage genetic medicines company focused on providing treatment for rare genetic diseases. The Company’s clinical programs include HMI-103, an investigational gene editing candidate in clinical development for the treatment of patients with phenylketonuria (PKU); HMI-203, an investigational gene therapy candidate in clinical development for the treatment of patients with mucopolysaccharidosis type II (MPS II), or Hunter syndrome; and HMI-102, an investigational gene therapy candidate in clinical development for the treatment of adult patients with PKU. Its lead GTx-mAb gene therapy candidate, HMI-104, for the treatment of patients with paroxysmal nocturnal hemoglobinuria (PNH). Its platform is designed to utilize human hematopoietic stem cell-derived adeno-associated virus vectors (AAVHSCs), to precisely and efficiently deliver single administration genetic medicines in vivo through a nuclease-free gene editing modality and gene therapy platform.
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